Participants taking 18 mg of nerandomilast experienced a significantly lower risk of acute exacerbation of interstitial lung disease. The US Food and Drug Administration (FDA) has approved ...
The majority (79%) of cardiac amyloidosis cases were responsible for sudden cardiac death. Cardiac amyloidosis can be associated with sudden cardiac death and is often undiagnosed during a person’s ...
Regional analysis showed the highest 2022 mortality in the Americas (1.80 per 100,000), followed by the Western Pacific (1.21) and Europe (1.11). Global mortality from idiopathic pulmonary fibrosis ...
The levels of proprotein convertase subtilisin/kexin type 9 could discriminate between male patients with primary sclerosing cholangitis and healthy controls and between female patients with PBC and ...
A banner welcomes delegates to the American College of Rheumatology’s 2025 conference in Chicago (Photo by Larry Luxner) The American College of Rheumatology awarded its 2025 Presidential Gold Medal ...
Cognitive impairment is a common manifestation of NMOSD; however, early diagnosis and prompt treatment can mitigate its effects. Cognition is one of the most fundamental functions of the human species ...
Allogeneic stem cell transplantation and targeted therapy conferred the longest median survival after HMA failure. Stem cell transplantation and targeted therapies were associated with markedly ...
Identifying a homozygous hotspot mutation in the CASP8 gene demonstrates that CED can underlie early-onset CIDP. A case involving a patient with early onset chronic inflammatory demyelinating ...
Protecting the quality of life in rare diseases, such as TK2d, through pain prevention should not be an afterthought of treatment. With many rare diseases, pain management eventually becomes a part of ...
Denecimig aims to help the body form blood clots more effectively by mimicking the role of FVIIIa and bridging factor IXa and factor X to restore thrombin generation and support normal clot formation.
Hospitalization was frequent, though lengths of stay varied, and polypharmacy was common among individuals with PWS. Prader-Willi syndrome (PWS) imposes a profound, multifaceted burden on patients, ...
Factors like platelet apoptosis and bioactive substances released during storage can influence immune responses. In Current Opinion in Immunology, researchers emphasized the importance of ...