In an interview-based study, adults with SMA reported a lack of coordination during their transition from pediatric care once ...

Nearly all children with spinal muscular atrophy who started on Evrysdi before symptom onset are walking after three years, ...

Columnist Helen Baldwin worried the baby who arrived May 18, 1997, would keep everyone awake, but his silence signaled a ...

Columnist Connie Chandler writes of a generational disconnect with new SMA patients, but says living fully must remain their ...

SMA Europe has launched an online tool designed to help patients, doctors, and others in the spinal muscular atrophy (SMA) ...

The exergame Tales from the Magic Keep aims to boost physical activity, and proved to be a feasible tool for children with ...

For people with spinal muscular atrophy, physical therapy can help support mobility, strength, and quality of life, regardless of SMA type.

Spinal muscular atrophy (SMA) is an inherited neurodegenerative disorder characterized by progressive muscle weakness. SMA patients do not produce enough of a protein called survival motor neuron (SMN ...

The gene therapy Zolgensma (onasemnogene abeparvovec-xioi) has been newly approved to treat patients with spinal muscular atrophy (SMA) through intravenous (IV) delivery, meaning systemically. However ...

In episode 153, host Kevin Schaefer talks with Annie Heathcote from Mazomanie, Wisconsin. Annie is a multi-business owner, social media… ...

Zolgensma, a first gene therapy for spinal muscular atrophy — and first for any chronic neurologic disease — is now an approved and potential “one-time” intravenous treatment for pre-symptomatic ...

Even though Ukraine has been at war for more than a year, a newborn screening program for spinal muscular atrophy (SMA) was launched late last year — and so far the program has successfully tested ...